His Story

Brayden

Team player, always

Born March 2015
Country United States
Diagnosis August 2018

A courageous boy who
never stopped fighting

Brayden was born in March 2015 and diagnosed with SMA-PME on August 10, 2018, at age 3 — and later with Farber disease at age 4. Both conditions stem from the same ASAH1 gene mutation, an overlap that makes his case particularly significant for research.

From the very beginning, Brayden faced medical challenges. He experienced multiple ear infections from birth, requiring tubes before his first birthday. Walking began at 17 months but was marked by frequent falls and a persistent clumsiness that caught the attention of his parents and doctors alike.

By ages 2 and 3, tremors emerged and his condition worsened significantly. A hospitalization for sudden inability to walk prompted extensive testing — including muscle biopsy and genetic testing with a neurological specialist in Rochester, New York — ultimately confirming SMA-PME. It was a devastating answer to years of worry, but it was also, finally, an answer.

Between ages 3 and 4, skin nodules appeared — a hallmark symptom of Farber disease — requiring skin biopsy and overseas consultation with specialists in France and Canada. By ages 4 and 5, throat nodules developed and Brayden received his first wheelchair. Seizures began at ages 5 and 6. By ages 6 and 7, respiratory infections escalated into aspiration pneumonia, leading to a feeding tube.

By ages 7 and 8, seizures had become a matter of daily life, and Brayden became completely wheelchair-dependent. Yet through every stage of his illness, his spirit has remained extraordinary. He loves baseball with a deep, undiminished passion — and those who know him describe him simply as "a very special and courageous boy."

Brayden's story is one of the clearest illustrations of why SMA-PME and Farber disease research are so deeply intertwined. Progress for one community is progress for both. He is the reason the work continues — and the reason it cannot stop.

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For Brayden.
For every child like him.

Brayden's courage in the face of SMA-PME and Farber disease is a daily inspiration. Your support helps fund the gene therapy research that could one day give children like him a different future.