Updated: November 20, 2025
Every dollar
funds hope.
Your contribution directly funds medical research and clinical trials targeting ASAH1 mutations that cause SMA-PME and Farber disease—ultra-rare genetic neurodegenerative conditions. We are a 501(c)(3) public charity, incorporated June 11, 2021, and approved as such on February 2, 2022.
No overhead. No administrative fees. Pure impact.
Our Impact
SMA-PME Research is dedicated to finding solutions for Spinal Muscular Atrophy with Progressive Myoclonic Epilepsy and related acid ceramidase deficiencies. Your donations fund:
- ✓ Medical Research & Clinical Trials — Direct funding for breakthrough research into ASAH1 mutations
- ✓ acDase Global Forums — International gatherings connecting families, physicians, and researchers
- ✓ Family Support Programs — Resources and community for families navigating diagnosis and treatment
Appreciation Gifts
Thank you for your generosity. Donors receive special appreciation items based on contribution level.
* Gifts available for US donations only; some exclusions apply.
Ways to Donate
For greatest convenience and optional fee (enter 0 at fee prompt), please consider a one-time or monthly recurring donation. Click the link to use any major credit card or transfer directly from your bank account, or scan the QR code.
zeffy.com/en-US/donation-form/donate-for-the-children-2 Donate via Zeffy
Donate securely via PayPal. One-time or recurring donations accepted using your PayPal account or any major credit card.
Donate via PayPalP.O. Box 50636
Myrtle Beach, SC 29579, USA
to the Extent of Law
🤝 Corporate Partnerships
SMA-PME Research seeks corporations that are interested in matching funds from their employees. Many corporate employers offer giving programs that can double your impact.